Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins. (Record no. 20528120)
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fixed length control field | 02181 a2200637 4500 |
005 - DATE AND TIME OF LATEST TRANSACTION | |
control field | 20250516021559.0 |
008 - FIXED-LENGTH DATA ELEMENTS--GENERAL INFORMATION | |
fixed length control field | 201111s 0 0 eng d |
022 ## - INTERNATIONAL STANDARD SERIAL NUMBER | |
International Standard Serial Number | 1525-0024 |
024 7# - OTHER STANDARD IDENTIFIER | |
Standard number or code | 10.1038/mt.2010.274 |
Source of number or code | doi |
040 ## - CATALOGING SOURCE | |
Original cataloging agency | NLM |
Language of cataloging | eng |
Transcribing agency | NLM |
100 1# - MAIN ENTRY--PERSONAL NAME | |
Personal name | Nathwani, Amit C |
264 #0 - PRODUCTION, PUBLICATION, DISTRIBUTION, MANUFACTURE, AND COPYRIGHT NOTICE | |
Date of production, publication, distribution, manufacture, or copyright notice | 20111102 |
245 00 - TITLE STATEMENT | |
Title | Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins. |
Medium | [electronic resource] |
260 ## - PUBLICATION, DISTRIBUTION, ETC. | |
Name of publisher, distributor, etc. | Molecular therapy : the journal of the American Society of Gene Therapy |
Date of publication, distribution, etc. | May 2011 |
300 ## - PHYSICAL DESCRIPTION | |
Extent | 876-85 p. |
Other physical details | digital |
500 ## - GENERAL NOTE | |
General note | Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Animals |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Capsid Proteins |
General subdivision | genetics |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Dependovirus |
General subdivision | genetics |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Factor IX |
General subdivision | genetics |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Gene Expression |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Genetic Therapy |
General subdivision | methods |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Genetic Vectors |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | HEK293 Cells |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Hemophilia B |
General subdivision | genetics |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Humans |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | In Situ Hybridization, Fluorescence |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Liver |
General subdivision | metabolism |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Macaca |
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
Topical term or geographic name entry element | Mice |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Rosales, Cecilia |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | McIntosh, Jenny |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Rastegarlari, Ghasem |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Nathwani, Devhrut |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Raj, Deepak |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Nawathe, Sushmita |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Waddington, Simon N |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Bronson, Roderick |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Jackson, Scott |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Donahue, Robert E |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | High, Katherine A |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Mingozzi, Federico |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Ng, Catherine Y C |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Zhou, Junfang |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Spence, Yunyu |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | McCarville, M Beth |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Valentine, Marc |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Allay, James |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Coleman, John |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Sleep, Susan |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Gray, John T |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Nienhuis, Arthur W |
700 1# - ADDED ENTRY--PERSONAL NAME | |
Personal name | Davidoff, Andrew M |
773 0# - HOST ITEM ENTRY | |
Title | Molecular therapy : the journal of the American Society of Gene Therapy |
Related parts | vol. 19 |
-- | no. 5 |
-- | p. 876-85 |
856 40 - ELECTRONIC LOCATION AND ACCESS | |
Uniform Resource Identifier | <a href="https://doi.org/10.1038/mt.2010.274">https://doi.org/10.1038/mt.2010.274</a> |
Public note | Available from publisher's website |
No items available.