Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial. (Record no. 19244548)
[ view plain ]
| 000 -LEADER | |
|---|---|
| fixed length control field | 02802 a2200889 4500 |
| 005 - DATE AND TIME OF LATEST TRANSACTION | |
| control field | 20250515192412.0 |
| 008 - FIXED-LENGTH DATA ELEMENTS--GENERAL INFORMATION | |
| fixed length control field | 200911s 0 0 eng d |
| 022 ## - INTERNATIONAL STANDARD SERIAL NUMBER | |
| International Standard Serial Number | 1474-547X |
| 024 7# - OTHER STANDARD IDENTIFIER | |
| Standard number or code | 10.1016/S0140-6736(09)61836-5 |
| Source of number or code | doi |
| 040 ## - CATALOGING SOURCE | |
| Original cataloging agency | NLM |
| Language of cataloging | eng |
| Transcribing agency | NLM |
| 100 1# - MAIN ENTRY--PERSONAL NAME | |
| Personal name | Maguire, Albert M |
| 264 #0 - PRODUCTION, PUBLICATION, DISTRIBUTION, MANUFACTURE, AND COPYRIGHT NOTICE | |
| Date of production, publication, distribution, manufacture, or copyright notice | 20091123 |
| 245 00 - TITLE STATEMENT | |
| Title | Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial. |
| Medium | [electronic resource] |
| 260 ## - PUBLICATION, DISTRIBUTION, ETC. | |
| Name of publisher, distributor, etc. | Lancet (London, England) |
| Date of publication, distribution, etc. | Nov 2009 |
| 300 ## - PHYSICAL DESCRIPTION | |
| Extent | 1597-605 p. |
| Other physical details | digital |
| 500 ## - GENERAL NOTE | |
| General note | Publication Type: Clinical Trial, Phase I; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Adolescent |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Adult |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Age Factors |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Blindness |
| General subdivision | congenital |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Carrier Proteins |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Child |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Dark Adaptation |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Dependovirus |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Disease Progression |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Dose-Response Relationship, Drug |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Electroretinography |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Eye Proteins |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Female |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Genetic Therapy |
| General subdivision | methods |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Genetic Vectors |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Humans |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Injections |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Male |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Mutation |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Nystagmus, Physiologic |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Optic Atrophy, Hereditary, Leber |
| General subdivision | diagnosis |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Safety |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Treatment Outcome |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Visual Acuity |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Young Adult |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | cis-trans-Isomerases |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | High, Katherine A |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Auricchio, Alberto |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Wright, J Fraser |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Pierce, Eric A |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Testa, Francesco |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Mingozzi, Federico |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Bennicelli, Jeannette L |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Ying, Gui-shuang |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Rossi, Settimio |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Fulton, Ann |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Marshall, Kathleen A |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Banfi, Sandro |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Chung, Daniel C |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Morgan, Jessica I W |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Hauck, Bernd |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Zelenaia, Olga |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Zhu, Xiaosong |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Raffini, Leslie |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Coppieters, Frauke |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | De Baere, Elfride |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Shindler, Kenneth S |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Volpe, Nicholas J |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Surace, Enrico M |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Acerra, Carmela |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Lyubarsky, Arkady |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Redmond, T Michael |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Stone, Edwin |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Sun, Junwei |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | McDonnell, Jennifer Wellman |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Leroy, Bart P |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Simonelli, Francesca |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Bennett, Jean |
| 773 0# - HOST ITEM ENTRY | |
| Title | Lancet (London, England) |
| Related parts | vol. 374 |
| -- | no. 9701 |
| -- | p. 1597-605 |
| 856 40 - ELECTRONIC LOCATION AND ACCESS | |
| Uniform Resource Identifier | <a href="https://doi.org/10.1016/S0140-6736(09)61836-5">https://doi.org/10.1016/S0140-6736(09)61836-5</a> |
| Public note | Available from publisher's website |
No items available.