Efficient engraftment of pluripotent stem cell-derived myogenic progenitors in a novel immunodeficient mouse model of limb girdle muscular dystrophy 2I.

Azzag, Karim

Efficient engraftment of pluripotent stem cell-derived myogenic progenitors in a novel immunodeficient mouse model of limb girdle muscular dystrophy 2I. [electronic resource] - Skeletal muscle 04 2020 - 10 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

2044-5040

10.1186/s13395-020-00228-3 doi


Animals
Cell Differentiation
Cells, Cultured
Dystroglycans--metabolism
Genetic Therapy--methods
Humans
Mice
Mice, Inbred C57BL
Mice, Inbred NOD
Mice, SCID
Muscle Fibers, Skeletal--cytology
Muscular Dystrophies, Limb-Girdle--genetics
PAX7 Transcription Factor--genetics
Pentosyltransferases--genetics
Pluripotent Stem Cells--cytology
Stem Cell Transplantation--methods