Combinatorial treatment for spinal muscular atrophy: An Editorial for 'Combined treatment with the histone deacetylase inhibitor LBH589 and a splice-switch antisense oligonucleotide enhances SMN2 splicing and SMN expression in Spinal Muscular Atrophy cells' on page 264.
Poletti, Angelo
Combinatorial treatment for spinal muscular atrophy: An Editorial for 'Combined treatment with the histone deacetylase inhibitor LBH589 and a splice-switch antisense oligonucleotide enhances SMN2 splicing and SMN expression in Spinal Muscular Atrophy cells' on page 264. [electronic resource] - Journal of neurochemistry 04 2020 - 146-149 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't; Comment
1471-4159
10.1111/jnc.14974 doi
Animals
Histone Deacetylase Inhibitors
Humans
Muscular Atrophy, Spinal
Oligonucleotides, Antisense
Panobinostat
RNA Splicing
Survival of Motor Neuron 2 Protein
Combinatorial treatment for spinal muscular atrophy: An Editorial for 'Combined treatment with the histone deacetylase inhibitor LBH589 and a splice-switch antisense oligonucleotide enhances SMN2 splicing and SMN expression in Spinal Muscular Atrophy cells' on page 264. [electronic resource] - Journal of neurochemistry 04 2020 - 146-149 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't; Comment
1471-4159
10.1111/jnc.14974 doi
Animals
Histone Deacetylase Inhibitors
Humans
Muscular Atrophy, Spinal
Oligonucleotides, Antisense
Panobinostat
RNA Splicing
Survival of Motor Neuron 2 Protein