Antisense oligonucleotide therapeutics in neurodegenerative diseases: the case of polyglutamine disorders.

Silva, Ana C

Antisense oligonucleotide therapeutics in neurodegenerative diseases: the case of polyglutamine disorders. [electronic resource] - Brain : a journal of neurology 02 2020 - 407-429 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review

1460-2156

10.1093/brain/awz328 doi


Animals
Humans
Huntingtin Protein--drug effects
Huntington Disease--drug therapy
Neurodegenerative Diseases--drug therapy
Oligonucleotides, Antisense--pharmacology
Peptides--genetics
Trinucleotide Repeat Expansion--genetics