Individualized treatment with denosumab in children with osteogenesis imperfecta - follow up of a trial cohort.
Hoyer-Kuhn, Heike
Individualized treatment with denosumab in children with osteogenesis imperfecta - follow up of a trial cohort. [electronic resource] - Orphanet journal of rare diseases 09 2019 - 219 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1750-1172
10.1186/s13023-019-1197-z doi
Bone Density--drug effects
Bone Density Conservation Agents--therapeutic use
Child
Collagen Type I--genetics
Collagen Type I, alpha 1 Chain
Denosumab--therapeutic use
Diphosphonates--therapeutic use
Female
Follow-Up Studies
Humans
Hypercalciuria--drug therapy
Male
Mutation--genetics
Osteogenesis Imperfecta--drug therapy
Retrospective Studies
Individualized treatment with denosumab in children with osteogenesis imperfecta - follow up of a trial cohort. [electronic resource] - Orphanet journal of rare diseases 09 2019 - 219 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1750-1172
10.1186/s13023-019-1197-z doi
Bone Density--drug effects
Bone Density Conservation Agents--therapeutic use
Child
Collagen Type I--genetics
Collagen Type I, alpha 1 Chain
Denosumab--therapeutic use
Diphosphonates--therapeutic use
Female
Follow-Up Studies
Humans
Hypercalciuria--drug therapy
Male
Mutation--genetics
Osteogenesis Imperfecta--drug therapy
Retrospective Studies