Using human Pompe disease-induced pluripotent stem cell-derived neural cells to identify compounds with therapeutic potential.
Huang, Hsiang-Po
Using human Pompe disease-induced pluripotent stem cell-derived neural cells to identify compounds with therapeutic potential. [electronic resource] - Human molecular genetics 12 2019 - 3880-3894 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1460-2083
10.1093/hmg/ddz218 doi
Animals
Azoles--administration & dosage
Blood-Brain Barrier
Brain--metabolism
Cell Culture Techniques
Cells, Cultured
Disease Models, Animal
Drug Evaluation, Preclinical
Female
Glycogen Storage Disease Type II--drug therapy
Gonanes--pharmacology
Humans
Induced Pluripotent Stem Cells--cytology
Injections, Intraperitoneal
Isoindoles
Male
Mice
Neural Stem Cells--cytology
Organoselenium Compounds--administration & dosage
Wortmannin--pharmacology
alpha-Glucosidases--genetics
Using human Pompe disease-induced pluripotent stem cell-derived neural cells to identify compounds with therapeutic potential. [electronic resource] - Human molecular genetics 12 2019 - 3880-3894 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1460-2083
10.1093/hmg/ddz218 doi
Animals
Azoles--administration & dosage
Blood-Brain Barrier
Brain--metabolism
Cell Culture Techniques
Cells, Cultured
Disease Models, Animal
Drug Evaluation, Preclinical
Female
Glycogen Storage Disease Type II--drug therapy
Gonanes--pharmacology
Humans
Induced Pluripotent Stem Cells--cytology
Injections, Intraperitoneal
Isoindoles
Male
Mice
Neural Stem Cells--cytology
Organoselenium Compounds--administration & dosage
Wortmannin--pharmacology
alpha-Glucosidases--genetics