Evaluating Benefit-risk Decision-making in Spinal Muscular Atrophy: A First-ever Study to Assess Risk Tolerance in the SMA Patient Community.

Cruz, Rosángel

Evaluating Benefit-risk Decision-making in Spinal Muscular Atrophy: A First-ever Study to Assess Risk Tolerance in the SMA Patient Community. [electronic resource] - Clinical therapeutics 05 2019 - 943-960.e4 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1879-114X

10.1016/j.clinthera.2019.03.012 doi


Adolescent
Adult
Caregivers--statistics & numerical data
Child
Child, Preschool
Decision Making
Disease Progression
Female
Humans
Infant
Male
Middle Aged
Muscular Atrophy, Spinal--therapy
Parents
Quality of Life
Risk Assessment
Surveys and Questionnaires
Young Adult