Outcome measures for children with mitochondrial disease: consensus recommendations for future studies from a Delphi-based international workshop.
Koene, Saskia
Outcome measures for children with mitochondrial disease: consensus recommendations for future studies from a Delphi-based international workshop. [electronic resource] - Journal of inherited metabolic disease 11 2018 - 1267-1273 p. digital
Publication Type: Consensus Development Conference; Journal Article; Research Support, Non-U.S. Gov't
1573-2665
10.1007/s10545-018-0229-5 doi
Child
Consensus
Delphi Technique
Humans
Internationality
Mitochondrial Encephalomyopathies--therapy
Mitochondrial Myopathies--therapy
Multicenter Studies as Topic
Muscle Development
Treatment Outcome
Validation Studies as Topic
Outcome measures for children with mitochondrial disease: consensus recommendations for future studies from a Delphi-based international workshop. [electronic resource] - Journal of inherited metabolic disease 11 2018 - 1267-1273 p. digital
Publication Type: Consensus Development Conference; Journal Article; Research Support, Non-U.S. Gov't
1573-2665
10.1007/s10545-018-0229-5 doi
Child
Consensus
Delphi Technique
Humans
Internationality
Mitochondrial Encephalomyopathies--therapy
Mitochondrial Myopathies--therapy
Multicenter Studies as Topic
Muscle Development
Treatment Outcome
Validation Studies as Topic