Long-term safety and efficacy of AAV gene therapy in the canine model of glycogen storage disease type Ia.

Lee, Young Mok

Long-term safety and efficacy of AAV gene therapy in the canine model of glycogen storage disease type Ia. [electronic resource] - Journal of inherited metabolic disease 11 2018 - 977-984 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1573-2665

10.1007/s10545-018-0199-7 doi


Animals
Blood Glucose--metabolism
Dependovirus--genetics
Disease Models, Animal
Dogs
Europe
Genetic Therapy--methods
Genetic Vectors
Glucose-6-Phosphatase--genetics
Glycogen Storage Disease Type I--therapy
Hypoglycemia--genetics
Kidney--metabolism
Liver--metabolism