Gene Therapy as a Curative Option for β-Thalassemia.

Biffi, Alessandra

Gene Therapy as a Curative Option for β-Thalassemia. [electronic resource] - The New England journal of medicine 04 2018 - 1551-1552 p. digital

Publication Type: Editorial; Comment

1533-4406

10.1056/NEJMe1802169 doi


Genetic Therapy
Genetic Vectors
Humans
Lentivirus--genetics
beta-Thalassemia