Worldwide study of hematopoietic allogeneic stem cell transplantation in pyruvate kinase deficiency.

van Straaten, Stephanie

Worldwide study of hematopoietic allogeneic stem cell transplantation in pyruvate kinase deficiency. [electronic resource] - Haematologica 02 2018 - e82-e86 p. digital

Publication Type: Journal Article

1592-8721

10.3324/haematol.2017.177857 doi


Adolescent
Adult
Anemia, Hemolytic--etiology
Anemia, Hemolytic, Congenital Nonspherocytic--complications
Child
Child, Preschool
Erythrocyte Transfusion
Female
Follow-Up Studies
Graft vs Host Disease--etiology
Hematopoietic Stem Cell Transplantation--adverse effects
Humans
Male
Pyruvate Kinase--deficiency
Pyruvate Metabolism, Inborn Errors--complications
Retrospective Studies
Survival Analysis
Young Adult