Hematopoietic stem cell transplantation rescues the hematological, immunological, and vascular phenotype in DADA2.

Hashem, Hasan

Hematopoietic stem cell transplantation rescues the hematological, immunological, and vascular phenotype in DADA2. [electronic resource] - Blood 12 2017 - 2682-2688 p. digital

Publication Type: Journal Article; Multicenter Study

1528-0020

10.1182/blood-2017-07-798660 doi


Adenosine Deaminase--blood
Adolescent
Child
Child, Preschool
Cohort Studies
Female
Graft vs Host Disease--diagnosis
Hematopoietic Stem Cell Transplantation--adverse effects
Humans
Immunologic Deficiency Syndromes--enzymology
Infant
Infant, Newborn
Intercellular Signaling Peptides and Proteins--blood
Male
Mutation
Phenotype
Transplantation Conditioning--methods