Retrospective study of long-term outcomes of enzyme replacement therapy in Fabry disease: Analysis of prognostic factors.

Arends, Maarten

Retrospective study of long-term outcomes of enzyme replacement therapy in Fabry disease: Analysis of prognostic factors. [electronic resource] - PloS one 2017 - e0182379 p. digital

Publication Type: Journal Article

1932-6203

10.1371/journal.pone.0182379 doi


Adolescent
Adult
Aged
Cardiovascular Diseases--complications
Comorbidity
Disease Progression
Enzyme Replacement Therapy--adverse effects
Fabry Disease--complications
Female
Glomerular Filtration Rate
Humans
Kidney--physiopathology
Male
Middle Aged
Multivariate Analysis
Phenotype
Prognosis
Proportional Hazards Models
Proteinuria--complications
Retrospective Studies
Risk Factors
Treatment Outcome
Triglycerides--blood
Young Adult