Incomplete biomarker response in mucopolysaccharidosis type I after successful hematopoietic cell transplantation.

Kuiper, Gé-Ann

Incomplete biomarker response in mucopolysaccharidosis type I after successful hematopoietic cell transplantation. [electronic resource] - Molecular genetics and metabolism 09 2017 - 86-91 p. digital

Publication Type: Journal Article

1096-7206

10.1016/j.ymgme.2017.05.009 doi


Biomarkers--analysis
Cell Transplantation
Child
Child, Preschool
Chromatography, Liquid
Dermatan Sulfate--analysis
Female
Hematopoietic Stem Cell Transplantation--adverse effects
Heparitin Sulfate--analysis
Humans
Infant
Infant, Newborn
Male
Mucopolysaccharidosis I--blood
Tandem Mass Spectrometry