Evaluation of Antisense Oligonucleotides Targeting ATXN3 in SCA3 Mouse Models.

Moore, Lauren R

Evaluation of Antisense Oligonucleotides Targeting ATXN3 in SCA3 Mouse Models. [electronic resource] - Molecular therapy. Nucleic acids Jun 2017 - 200-210 p. digital

Publication Type: Journal Article

2162-2531

10.1016/j.omtn.2017.04.005 doi