Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome.
Gadalla, Kamal K E
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome. [electronic resource] - Molecular therapy. Methods & clinical development Jun 2017 - 180-190 p. digital
Publication Type: Journal Article
2329-0501
10.1016/j.omtm.2017.04.007 doi
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome. [electronic resource] - Molecular therapy. Methods & clinical development Jun 2017 - 180-190 p. digital
Publication Type: Journal Article
2329-0501
10.1016/j.omtm.2017.04.007 doi