In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model.
Mattar, Citra N Z
In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy 08 2017 - 1843-1853 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1525-0024
10.1016/j.ymthe.2017.04.003 doi
Animals
Antibodies, Neutralizing--immunology
Antibodies, Viral--blood
Dependovirus--genetics
Disease Models, Animal
Factor IX--genetics
Female
Gene Expression
Gene Transfer Techniques
Genetic Therapy
Genetic Vectors--administration & dosage
Hemophilia B--blood
Humans
Immune Tolerance
Liver--metabolism
Macaca fascicularis
Male
Pregnancy
Time Factors
Transduction, Genetic
Transgenes
In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy 08 2017 - 1843-1853 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1525-0024
10.1016/j.ymthe.2017.04.003 doi
Animals
Antibodies, Neutralizing--immunology
Antibodies, Viral--blood
Dependovirus--genetics
Disease Models, Animal
Factor IX--genetics
Female
Gene Expression
Gene Transfer Techniques
Genetic Therapy
Genetic Vectors--administration & dosage
Hemophilia B--blood
Humans
Immune Tolerance
Liver--metabolism
Macaca fascicularis
Male
Pregnancy
Time Factors
Transduction, Genetic
Transgenes