Lentiviral vectors can be used for full-length dystrophin gene therapy.

Counsell, John R

Lentiviral vectors can be used for full-length dystrophin gene therapy. [electronic resource] - Scientific reports 03 2017 - 79 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

2045-2322

10.1038/s41598-017-00152-5 doi


Cells, Cultured
DNA Packaging
Dystrophin--genetics
Genetic Therapy
Genetic Vectors--genetics
HEK293 Cells
HeLa Cells
Humans
Lentivirus--genetics
Muscular Dystrophy, Duchenne--genetics
Myoblasts, Skeletal--metabolism
Recombination, Genetic
Transduction, Genetic