An AAVrh10-CAG-CYP21-HA vector allows persistent correction of 21-hydroxylase deficiency in a Cyp21

Perdomini, M

An AAVrh10-CAG-CYP21-HA vector allows persistent correction of 21-hydroxylase deficiency in a Cyp21 [electronic resource] - Gene therapy 05 2017 - 275-281 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1476-5462

10.1038/gt.2017.10 doi


Adrenal Cortex--metabolism
Adrenal Hyperplasia, Congenital--genetics
Adrenocorticotropic Hormone--metabolism
Animals
Body Weight
Cell Line, Tumor
Dependovirus--genetics
Genetic Therapy--methods
Genetic Vectors--genetics
Humans
Mice
Progesterone--blood
Steroid 21-Hydroxylase--genetics