Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study.
Hughes, Derralynn A
Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study. [electronic resource] - Journal of medical genetics 04 2017 - 288-296 p. digital
Publication Type: Clinical Trial, Phase III; Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
1468-6244
10.1136/jmedgenet-2016-104178 doi
1-Deoxynojirimycin--administration & dosage
Administration, Oral
Adolescent
Adult
Aged
Enzyme Replacement Therapy--adverse effects
Fabry Disease--drug therapy
Female
Humans
Lysosomes--genetics
Male
Middle Aged
Molecular Chaperones--administration & dosage
Treatment Outcome
alpha-Galactosidase--genetics
Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study. [electronic resource] - Journal of medical genetics 04 2017 - 288-296 p. digital
Publication Type: Clinical Trial, Phase III; Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
1468-6244
10.1136/jmedgenet-2016-104178 doi
1-Deoxynojirimycin--administration & dosage
Administration, Oral
Adolescent
Adult
Aged
Enzyme Replacement Therapy--adverse effects
Fabry Disease--drug therapy
Female
Humans
Lysosomes--genetics
Male
Middle Aged
Molecular Chaperones--administration & dosage
Treatment Outcome
alpha-Galactosidase--genetics