Novel HDAd/EBV Reprogramming Vector and Highly Efficient Ad/CRISPR-Cas Sickle Cell Disease Gene Correction.

Li, Chao

Novel HDAd/EBV Reprogramming Vector and Highly Efficient Ad/CRISPR-Cas Sickle Cell Disease Gene Correction. [electronic resource] - Scientific reports 07 2016 - 30422 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

2045-2322

10.1038/srep30422 doi


Adenoviridae--metabolism
Anemia, Sickle Cell--genetics
Base Sequence
CRISPR-Cas Systems--genetics
Cell Line
Genetic Therapy
Genetic Vectors--metabolism
Helper Viruses--metabolism
Herpesvirus 4, Human
Homozygote
Humans
Induced Pluripotent Stem Cells--metabolism