Accessing the accelerated approval pathway for rare disease therapeutics.

Kakkis, Emil D

Accessing the accelerated approval pathway for rare disease therapeutics. [electronic resource] - Nature biotechnology Apr 2016 - 380-3 p. digital

Publication Type: Journal Article

1546-1696

10.1038/nbt.3530 doi


Biomarkers--analysis
Drug Approval--legislation & jurisprudence
Humans
Rare Diseases--diagnosis
United States
United States Food and Drug Administration