Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?

Cavazzana, Marina

Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand? [electronic resource] - Human gene therapy Feb 2016 - 108-16 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review

1557-7422

10.1089/hum.2015.137 doi


B-Lymphocytes--immunology
Clinical Trials as Topic
Gammaretrovirus--genetics
Genetic Therapy--methods
Genetic Vectors--chemistry
Hematopoietic Stem Cell Transplantation
Hematopoietic Stem Cells--cytology
Humans
Killer Cells, Natural--immunology
Lentivirus--genetics
Patient Safety
Retroviridae--genetics
T-Lymphocytes--immunology
Virus Integration--genetics
X-Linked Combined Immunodeficiency Diseases--genetics