Protein Delivery of an Artificial Transcription Factor Restores Widespread Ube3a Expression in an Angelman Syndrome Mouse Brain.

Bailus, Barbara J

Protein Delivery of an Artificial Transcription Factor Restores Widespread Ube3a Expression in an Angelman Syndrome Mouse Brain. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Mar 2016 - 548-55 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

1525-0024

10.1038/mt.2015.236 doi


Angelman Syndrome--genetics
Animals
Blood-Brain Barrier--metabolism
Brain--metabolism
Disease Models, Animal
Gene Expression
Gene Expression Regulation
Genes, Reporter
Genetic Loci
Mice
Transcription Factors--administration & dosage
Ubiquitin-Protein Ligases--genetics
Zinc Fingers