Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector.
Choudhury, Sourav R
Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Apr 2016 - 726-35 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0024
10.1038/mt.2015.231 doi
Animals
CHO Cells
Capsid Proteins--genetics
Cats
Cell Line
Central Nervous System--metabolism
Cricetulus
Dependovirus--genetics
Gene Transfer Techniques
Genetic Therapy
Genetic Vectors--administration & dosage
Huntingtin Protein--antagonists & inhibitors
Mice
Peptides--genetics
Recombinant Fusion Proteins--metabolism
Transduction, Genetic
Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Apr 2016 - 726-35 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0024
10.1038/mt.2015.231 doi
Animals
CHO Cells
Capsid Proteins--genetics
Cats
Cell Line
Central Nervous System--metabolism
Cricetulus
Dependovirus--genetics
Gene Transfer Techniques
Genetic Therapy
Genetic Vectors--administration & dosage
Huntingtin Protein--antagonists & inhibitors
Mice
Peptides--genetics
Recombinant Fusion Proteins--metabolism
Transduction, Genetic