Thalassemia Modular Stratification System for Personalized Therapy of Beta-Thalassemia (THALAMOSS).

Thalassemia Modular Stratification System for Personalized Therapy of Beta-Thalassemia (THALAMOSS). [electronic resource] - Human gene therapy. Clinical development Jun 2015 - 100-2 p. digital

Publication Type: Journal Article

2324-8645

10.1089/humc.2015.2530 doi


Biomarkers
Genetic Therapy
Genomics
Genotype
Humans
Mutation
Precision Medicine
beta-Globins--genetics
beta-Thalassemia--genetics