Rescue of gene-expression changes in an induced mouse model of spinal muscular atrophy by an antisense oligonucleotide that promotes inclusion of SMN2 exon 7.

Staropoli, John F

Rescue of gene-expression changes in an induced mouse model of spinal muscular atrophy by an antisense oligonucleotide that promotes inclusion of SMN2 exon 7. [electronic resource] - Genomics Apr 2015 - 220-8 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1089-8646

10.1016/j.ygeno.2015.01.007 doi


Animals
Disease Models, Animal
Exons
Gene Expression--drug effects
Mice
Muscular Atrophy, Spinal--drug therapy
Oligonucleotides, Antisense--pharmacology
Spinal Cord--drug effects
Survival of Motor Neuron 2 Protein--drug effects