Adeno-associated virus vector-based gene therapy for monogenetic metabolic diseases of the liver.
Junge, Norman
Adeno-associated virus vector-based gene therapy for monogenetic metabolic diseases of the liver. [electronic resource] - Journal of pediatric gastroenterology and nutrition Apr 2015 - 433-40 p. digital
Publication Type: Journal Article; Review
1536-4801
10.1097/MPG.0000000000000703 doi
Dependovirus--genetics
Genetic Therapy
Genetic Vectors
Humans
Liver Diseases--metabolism
Metabolic Diseases--therapy
Adeno-associated virus vector-based gene therapy for monogenetic metabolic diseases of the liver. [electronic resource] - Journal of pediatric gastroenterology and nutrition Apr 2015 - 433-40 p. digital
Publication Type: Journal Article; Review
1536-4801
10.1097/MPG.0000000000000703 doi
Dependovirus--genetics
Genetic Therapy
Genetic Vectors
Humans
Liver Diseases--metabolism
Metabolic Diseases--therapy