Restoration of progranulin expression rescues cortical neuron generation in an induced pluripotent stem cell model of frontotemporal dementia.

Raitano, Susanna

Restoration of progranulin expression rescues cortical neuron generation in an induced pluripotent stem cell model of frontotemporal dementia. [electronic resource] - Stem cell reports Jan 2015 - 16-24 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

2213-6711

10.1016/j.stemcr.2014.12.001 doi


Biomarkers
Cell Differentiation
Cell Line
Frontotemporal Dementia--genetics
Gene Expression
Gene Expression Profiling
Haploinsufficiency
Humans
Induced Pluripotent Stem Cells--cytology
Intercellular Signaling Peptides and Proteins--genetics
Mutation
Neural Stem Cells--cytology
Neurogenesis--genetics
Neurons--metabolism
Phenotype
Progranulins
Time Factors
Transcription, Genetic
Transcriptome
Wnt Signaling Pathway