Long-term safety and efficacy of factor IX gene therapy in hemophilia B.
Nathwani, Amit C
Long-term safety and efficacy of factor IX gene therapy in hemophilia B. [electronic resource] - The New England journal of medicine Nov 2014 - 1994-2004 p. digital
Publication Type: Clinical Trial, Phase I; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1533-4406
10.1056/NEJMoa1407309 doi
Adult
Alanine Transaminase--blood
Dependovirus--genetics
Factor IX--genetics
Follow-Up Studies
Gene Expression
Genetic Therapy--adverse effects
Genetic Vectors--administration & dosage
Hemophilia B--blood
Humans
Infusions, Intravenous
Male
Middle Aged
Transgenes
Young Adult
Long-term safety and efficacy of factor IX gene therapy in hemophilia B. [electronic resource] - The New England journal of medicine Nov 2014 - 1994-2004 p. digital
Publication Type: Clinical Trial, Phase I; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1533-4406
10.1056/NEJMoa1407309 doi
Adult
Alanine Transaminase--blood
Dependovirus--genetics
Factor IX--genetics
Follow-Up Studies
Gene Expression
Genetic Therapy--adverse effects
Genetic Vectors--administration & dosage
Hemophilia B--blood
Humans
Infusions, Intravenous
Male
Middle Aged
Transgenes
Young Adult