Mucopolysaccharidosis type I.

Wraith, J E

Mucopolysaccharidosis type I. [electronic resource] - Pediatric endocrinology reviews : PER Sep 2014 - 102-6 p. digital

Publication Type: Journal Article; Review

1565-4753


Combined Modality Therapy
Enzyme Replacement Therapy
Hematopoietic Stem Cell Transplantation
Humans
Iduronidase--therapeutic use
Mucopolysaccharidosis I--diagnosis
Treatment Outcome