Observational study of spinal muscular atrophy type I and implications for clinical trials.

Finkel, Richard S

Observational study of spinal muscular atrophy type I and implications for clinical trials. [electronic resource] - Neurology Aug 2014 - 810-7 p. digital

Publication Type: Journal Article; Multicenter Study; Observational Study; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

1526-632X

10.1212/WNL.0000000000000741 doi


Cohort Studies
Female
Humans
Infant
Male
Research Design
Spinal Muscular Atrophies of Childhood