Nonmyeloablative HLA-matched sibling allogeneic hematopoietic stem cell transplantation for severe sickle cell phenotype.
Hsieh, Matthew M
Nonmyeloablative HLA-matched sibling allogeneic hematopoietic stem cell transplantation for severe sickle cell phenotype. [electronic resource] - JAMA Jul 2014 - 48-56 p. digital
Publication Type: Clinical Trial; Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Research Support, N.I.H., Intramural
1538-3598
10.1001/jama.2014.7192 doi
Adolescent
Adult
Aged
Alemtuzumab
Anemia, Sickle Cell--complications
Antibodies, Monoclonal, Humanized--administration & dosage
Chimerism
Erythrocytes
Female
Filgrastim
Graft vs Host Disease
Granulocyte Colony-Stimulating Factor
HLA Antigens
Hematopoietic Stem Cell Mobilization
Hematopoietic Stem Cell Transplantation--adverse effects
Humans
Immunosuppressive Agents--administration & dosage
Infections--etiology
Male
Middle Aged
Pain--etiology
Prospective Studies
Recombinant Proteins
Sirolimus--administration & dosage
Transplantation Conditioning
Transplantation, Homologous
Treatment Outcome
Whole-Body Irradiation
Young Adult
beta-Thalassemia--complications
Nonmyeloablative HLA-matched sibling allogeneic hematopoietic stem cell transplantation for severe sickle cell phenotype. [electronic resource] - JAMA Jul 2014 - 48-56 p. digital
Publication Type: Clinical Trial; Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Research Support, N.I.H., Intramural
1538-3598
10.1001/jama.2014.7192 doi
Adolescent
Adult
Aged
Alemtuzumab
Anemia, Sickle Cell--complications
Antibodies, Monoclonal, Humanized--administration & dosage
Chimerism
Erythrocytes
Female
Filgrastim
Graft vs Host Disease
Granulocyte Colony-Stimulating Factor
HLA Antigens
Hematopoietic Stem Cell Mobilization
Hematopoietic Stem Cell Transplantation--adverse effects
Humans
Immunosuppressive Agents--administration & dosage
Infections--etiology
Male
Middle Aged
Pain--etiology
Prospective Studies
Recombinant Proteins
Sirolimus--administration & dosage
Transplantation Conditioning
Transplantation, Homologous
Treatment Outcome
Whole-Body Irradiation
Young Adult
beta-Thalassemia--complications