NIM811, a cyclophilin inhibitor without immunosuppressive activity, is beneficial in collagen VI congenital muscular dystrophy models.
Zulian, Alessandra
NIM811, a cyclophilin inhibitor without immunosuppressive activity, is beneficial in collagen VI congenital muscular dystrophy models. [electronic resource] - Human molecular genetics Oct 2014 - 5353-63 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1460-2083
10.1093/hmg/ddu254 doi
Animals
Apoptosis--drug effects
Cells, Cultured
Collagen Type VI--genetics
Cyclosporine--administration & dosage
Disease Models, Animal
Humans
Mice
Mitochondria--metabolism
Muscle Strength--drug effects
Muscular Dystrophies--congenital
Zebrafish
Zebrafish Proteins--genetics
NIM811, a cyclophilin inhibitor without immunosuppressive activity, is beneficial in collagen VI congenital muscular dystrophy models. [electronic resource] - Human molecular genetics Oct 2014 - 5353-63 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1460-2083
10.1093/hmg/ddu254 doi
Animals
Apoptosis--drug effects
Cells, Cultured
Collagen Type VI--genetics
Cyclosporine--administration & dosage
Disease Models, Animal
Humans
Mice
Mitochondria--metabolism
Muscle Strength--drug effects
Muscular Dystrophies--congenital
Zebrafish
Zebrafish Proteins--genetics