Lysosomal storage disorders: old diseases, present and future challenges.

Klein, Andrés D

Lysosomal storage disorders: old diseases, present and future challenges. [electronic resource] - Pediatric endocrinology reviews : PER Nov 2013 - 59-63 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review

1565-4753


Animals
Genetic Predisposition to Disease
Genetic Therapy--methods
Global Health
Humans
Incidence
Leukocyte Elastase--deficiency
Lysosomal Storage Diseases--epidemiology
Phenotype