Lysosomal storage disorders: old diseases, present and future challenges.
Klein, Andrés D
Lysosomal storage disorders: old diseases, present and future challenges. [electronic resource] - Pediatric endocrinology reviews : PER Nov 2013 - 59-63 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review
1565-4753
Animals
Genetic Predisposition to Disease
Genetic Therapy--methods
Global Health
Humans
Incidence
Leukocyte Elastase--deficiency
Lysosomal Storage Diseases--epidemiology
Phenotype
Lysosomal storage disorders: old diseases, present and future challenges. [electronic resource] - Pediatric endocrinology reviews : PER Nov 2013 - 59-63 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review
1565-4753
Animals
Genetic Predisposition to Disease
Genetic Therapy--methods
Global Health
Humans
Incidence
Leukocyte Elastase--deficiency
Lysosomal Storage Diseases--epidemiology
Phenotype