Repurposing diflunisal for familial amyloid polyneuropathy: a randomized clinical trial.
Berk, John L
Repurposing diflunisal for familial amyloid polyneuropathy: a randomized clinical trial. [electronic resource] - JAMA Dec 2013 - 2658-67 p. digital
Publication Type: Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
1538-3598
10.1001/jama.2013.283815 doi
Aged
Amyloid Neuropathies, Familial--drug therapy
Anti-Inflammatory Agents, Non-Steroidal--therapeutic use
Body Mass Index
Diflunisal--therapeutic use
Disease Progression
Double-Blind Method
Female
Humans
Male
Middle Aged
Quality of Life
Survival Analysis
Treatment Outcome
Repurposing diflunisal for familial amyloid polyneuropathy: a randomized clinical trial. [electronic resource] - JAMA Dec 2013 - 2658-67 p. digital
Publication Type: Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
1538-3598
10.1001/jama.2013.283815 doi
Aged
Amyloid Neuropathies, Familial--drug therapy
Anti-Inflammatory Agents, Non-Steroidal--therapeutic use
Body Mass Index
Diflunisal--therapeutic use
Disease Progression
Double-Blind Method
Female
Humans
Male
Middle Aged
Quality of Life
Survival Analysis
Treatment Outcome