Antisense oligonucleotide treatment ameliorates alpha-1 antitrypsin-related liver disease in mice.

Guo, Shuling

Antisense oligonucleotide treatment ameliorates alpha-1 antitrypsin-related liver disease in mice. [electronic resource] - The Journal of clinical investigation Jan 2014 - 251-61 p. digital

Publication Type: Journal Article

1558-8238

10.1172/JCI67968 doi


Animals
Female
Gene Knockdown Techniques
Hep G2 Cells
Hepatocytes--enzymology
Humans
Liver--enzymology
Liver Cirrhosis--enzymology
Macaca fascicularis
Male
Mice
Mice, Transgenic
Oligonucleotides, Antisense--genetics
RNA, Messenger--genetics
alpha 1-Antitrypsin--genetics
alpha 1-Antitrypsin Deficiency--enzymology