Enzyme replacement therapy with laronidase (Aldurazyme) for treating mucopolysaccharidosis type I.
Jameson, Elisabeth
Enzyme replacement therapy with laronidase (Aldurazyme) for treating mucopolysaccharidosis type I. [electronic resource] - The Cochrane database of systematic reviews Sep 2013 - CD009354 p. digital
Publication Type: Journal Article; Review; Systematic Review
1469-493X
10.1002/14651858.CD009354.pub2 doi
Enzyme Replacement Therapy--methods
Humans
Iduronidase--administration & dosage
Mucopolysaccharidosis I--classification
Randomized Controlled Trials as Topic
Rare Diseases--classification
Enzyme replacement therapy with laronidase (Aldurazyme) for treating mucopolysaccharidosis type I. [electronic resource] - The Cochrane database of systematic reviews Sep 2013 - CD009354 p. digital
Publication Type: Journal Article; Review; Systematic Review
1469-493X
10.1002/14651858.CD009354.pub2 doi
Enzyme Replacement Therapy--methods
Humans
Iduronidase--administration & dosage
Mucopolysaccharidosis I--classification
Randomized Controlled Trials as Topic
Rare Diseases--classification