Cardiac α-actin over-expression therapy in dominant ACTA1 disease.

Ravenscroft, Gianina

Cardiac α-actin over-expression therapy in dominant ACTA1 disease. [electronic resource] - Human molecular genetics Oct 2013 - 3987-97 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1460-2083

10.1093/hmg/ddt252 doi


Actins--genetics
Animals
Disease Models, Animal
Female
Genes, Recessive
Genetic Therapy
Humans
Male
Mice
Mice, Knockout
Muscle, Skeletal--metabolism
Muscular Diseases--genetics
Mutation
Myocardium--metabolism
Phenotype