Gene therapy for misfolding protein diseases of the central nervous system.
San Sebastian, Waldy
Gene therapy for misfolding protein diseases of the central nervous system. [electronic resource] - Neurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics Jul 2013 - 498-510 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Review
1878-7479
10.1007/s13311-013-0191-8 doi
Animals
Central Nervous System Diseases--complications
Genetic Therapy--methods
Humans
Proteostasis Deficiencies--complications
Gene therapy for misfolding protein diseases of the central nervous system. [electronic resource] - Neurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics Jul 2013 - 498-510 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Review
1878-7479
10.1007/s13311-013-0191-8 doi
Animals
Central Nervous System Diseases--complications
Genetic Therapy--methods
Humans
Proteostasis Deficiencies--complications