Efficacy and safety of ivacaftor in patients aged 6 to 11 years with cystic fibrosis with a G551D mutation.

Davies, Jane C

Efficacy and safety of ivacaftor in patients aged 6 to 11 years with cystic fibrosis with a G551D mutation. [electronic resource] - American journal of respiratory and critical care medicine Jun 2013 - 1219-25 p. digital

Publication Type: Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, Non-U.S. Gov't

1535-4970

10.1164/rccm.201301-0153OC doi


Administration, Oral
Alleles
Aminophenols--administration & dosage
Child
Cystic Fibrosis--drug therapy
Cystic Fibrosis Transmembrane Conductance Regulator--genetics
DNA--genetics
Dose-Response Relationship, Drug
Double-Blind Method
Forced Expiratory Volume
Humans
Lung--physiopathology
Mutation
Quinolones--administration & dosage
Respiratory Function Tests
Treatment Outcome