Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement.
Cideciyan, Artur V
Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement. [electronic resource] - Proceedings of the National Academy of Sciences of the United States of America Feb 2013 - E517-25 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1091-6490
10.1073/pnas.1218933110 doi
Adolescent
Adult
Animals
Child
Child, Preschool
Disease Models, Animal
Dogs
Genetic Therapy
Humans
Leber Congenital Amaurosis--genetics
Mutation
Photoreceptor Cells, Vertebrate--pathology
Retinal Degeneration--genetics
Time Factors
Vision, Ocular
Young Adult
cis-trans-Isomerases--genetics
Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement. [electronic resource] - Proceedings of the National Academy of Sciences of the United States of America Feb 2013 - E517-25 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1091-6490
10.1073/pnas.1218933110 doi
Adolescent
Adult
Animals
Child
Child, Preschool
Disease Models, Animal
Dogs
Genetic Therapy
Humans
Leber Congenital Amaurosis--genetics
Mutation
Photoreceptor Cells, Vertebrate--pathology
Retinal Degeneration--genetics
Time Factors
Vision, Ocular
Young Adult
cis-trans-Isomerases--genetics