New strategies for the treatment of lysosomal storage diseases (review).
Parenti, Giancarlo
New strategies for the treatment of lysosomal storage diseases (review). [electronic resource] - International journal of molecular medicine Jan 2013 - 11-20 p. digital
Publication Type: Journal Article; Review
1791-244X
10.3892/ijmm.2012.1187 doi
Animals
Disease Models, Animal
Enzyme Replacement Therapy--methods
Genetic Therapy--methods
Hematopoietic Stem Cell Transplantation--methods
Humans
Hydrolases--metabolism
Lysosomal Storage Diseases--genetics
Lysosomes--metabolism
Molecular Chaperones--metabolism
Proteostasis Deficiencies--therapy
New strategies for the treatment of lysosomal storage diseases (review). [electronic resource] - International journal of molecular medicine Jan 2013 - 11-20 p. digital
Publication Type: Journal Article; Review
1791-244X
10.3892/ijmm.2012.1187 doi
Animals
Disease Models, Animal
Enzyme Replacement Therapy--methods
Genetic Therapy--methods
Hematopoietic Stem Cell Transplantation--methods
Humans
Hydrolases--metabolism
Lysosomal Storage Diseases--genetics
Lysosomes--metabolism
Molecular Chaperones--metabolism
Proteostasis Deficiencies--therapy