New motor outcome function measures in evaluation of late-onset Pompe disease before and after enzyme replacement therapy.

Angelini, Corrado

New motor outcome function measures in evaluation of late-onset Pompe disease before and after enzyme replacement therapy. [electronic resource] - Muscle & nerve Jun 2012 - 831-4 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1097-4598

10.1002/mus.23340 doi


Adult
Age of Onset
Aged
Disability Evaluation
Enzyme Replacement Therapy
Female
Follow-Up Studies
Gait--physiology
Glycogen Storage Disease Type II--drug therapy
Humans
Male
Middle Aged
Motor Activity--physiology
Outcome Assessment, Health Care
Treatment Outcome
Walking--physiology