Gene therapy rescues photoreceptor blindness in dogs and paves the way for treating human X-linked retinitis pigmentosa.

Beltran, William A

Gene therapy rescues photoreceptor blindness in dogs and paves the way for treating human X-linked retinitis pigmentosa. [electronic resource] - Proceedings of the National Academy of Sciences of the United States of America Feb 2012 - 2132-7 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1091-6490

10.1073/pnas.1118847109 doi


Animals
Blindness--genetics
Dogs
Eye Proteins--genetics
Genetic Diseases, X-Linked--genetics
Genetic Therapy
Genotype
Humans
Mice
Mutation--genetics
Open Reading Frames--genetics
Opsins--metabolism
Phenotype
Photoreceptor Cells, Vertebrate--pathology
Protein Transport
Retinal Bipolar Cells--pathology
Retinitis Pigmentosa--genetics