Impending therapies for Duchenne muscular dystrophy.

Partridge, Terence A

Impending therapies for Duchenne muscular dystrophy. [electronic resource] - Current opinion in neurology Oct 2011 - 415-22 p. digital

Publication Type: Journal Article; Review

1473-6551

10.1097/WCO.0b013e32834aa3f1 doi


Forecasting
Gene Transfer Techniques
Genetic Therapy--methods
Genetic Vectors--therapeutic use
Humans
Muscular Dystrophy, Duchenne--genetics
Stem Cells
Targeted Gene Repair