Lentiviral-mediated gene transfer to the sheep brain: implications for gene therapy in Batten disease.

Linterman, Kathryn S

Lentiviral-mediated gene transfer to the sheep brain: implications for gene therapy in Batten disease. [electronic resource] - Human gene therapy Aug 2011 - 1011-20 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1557-7422

10.1089/hum.2011.026 doi


Animals
Brain--metabolism
Gene Transfer Techniques
Genetic Therapy
Green Fluorescent Proteins--genetics
Lentivirus--genetics
Neuronal Ceroid-Lipofuscinoses--genetics
Neurons--metabolism
Sheep
Transgenes