Systemic adeno-associated virus-mediated gene therapy preserves retinal ganglion cells and visual function in DBA/2J glaucomatous mice.

Sullivan, Timothy A

Systemic adeno-associated virus-mediated gene therapy preserves retinal ganglion cells and visual function in DBA/2J glaucomatous mice. [electronic resource] - Human gene therapy Oct 2011 - 1191-200 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

1557-7422

10.1089/hum.2011.052 doi


Analysis of Variance
Animals
Axons--drug effects
Dependovirus
Enzyme-Linked Immunosorbent Assay
Erythropoietin--administration & dosage
Evoked Potentials, Visual--physiology
Genetic Therapy--methods
Genetic Vectors--administration & dosage
Glaucoma--genetics
Hematocrit
Immunohistochemistry
Injections, Intramuscular
Macaca mulatta--genetics
Mice
Mice, Inbred DBA
Mutation, Missense--genetics
Optic Nerve--drug effects
Retinal Ganglion Cells--drug effects
Vision, Ocular--drug effects