Trans-splicing, more than meets the eye: multifaceted therapeutics for spinal muscular atrophy.

Butchbach, Matthew E R

Trans-splicing, more than meets the eye: multifaceted therapeutics for spinal muscular atrophy. [electronic resource] - Human gene therapy Feb 2011 - 121-5 p. digital

Publication Type: Comment; Journal Article

1557-7422

10.1089/hum.2011.903 doi


Animals
Gene Expression
Genetic Therapy
Humans
Insulin-Like Growth Factor I--metabolism
Mice
Mice, Transgenic
Muscular Atrophy, Spinal--genetics
Survival of Motor Neuron 1 Protein--genetics
Survival of Motor Neuron 2 Protein--genetics
Trans-Splicing